Hemophilia
Factor mimetics, gene therapy durability, and rebalancing agents.
Lenses
EarlierApproval →
PFEApprovedcash ok
2026-11-20 (99d)Estimated
Beqvez gene therapy · NCT04323098 · Uptake / durability update
BMRNApprovedcash ok
2026-10-01 (49d)Company-guided
Roctavian · NCT03392974 · Commercial update
NVOFiledcash ok
2026-08-29 (16d)Confirmed
Mim8 factor mimetic · NCT05053139 · PDUFA — Mim8
SGMOPh3cash tight
2026-12-18 (127d)Estimated
Giroctocogene fitelparvovec · NCT04370054 · Partnered Ph3 update